Nicole Verdun, MD, super office director of the FDA’s Office of Therapeutic Products (OTP) and her deputy Rachael Anatol, PhD ...

He was diagnosed with Duchenne muscular dystrophy at age 5.Family remembers the day everything changed"I can remember the day ...

A North Texas family is sharing a son's journey with Duchenne muscular dystrophy, a rare and progressive muscle-wasting ...

Sarepta shares face pressure after a second Elevidys-linked death and analyst downgrade over safety concerns and lowered ...

The ouster of the FDA's chief regulator of cell and gene therapies came immediately after a disagreement with her boss over a ...

The Kansas City Chiefs welcomed some special guests to their mandatory minicamp on Tuesday, June 17, and Patrick Mahomes and ...

“Giancarlo (Stanton) was probably the scariest guy that I’ve ever faced,” Fried said. “I’ve been on the mound and all I could ...

NEW YORK – Carmine and Vincent Gagliano, two brothers from Brooklyn, were living the dream on Thursday at Yankee Stadium. It ...

Duchenne muscular dystrophy families are sharing stories about Elevidys complications on social media. But they aren’t ...